Language

English

Publication Date

8-20-2025

Journal

Acta Neuropathologica Communications

DOI

10.1186/s40478-025-02098-6

PMID

40836245

PMCID

PMC12366115

PubMedCentral® Posted Date

8-20-2025

PubMedCentral® Full Text Version

Post-print

Abstract

Background: Germline Structural Variants (SVs) represent an important source of genetic diversity, in large part due to their influence on gene transcription. It is necessary to systematically catalog germline SVs and their associated impacted genes across different cohorts and tissue and cellular contexts, including pediatric brain or Central Nervous System (CNS) tumors.

Methods: We combined RNA with whole genome sequencing across 1430 pediatric brain or CNS tumor patients from the Children's Brain Tumor Network. We set out to systematically identify genes for which the proximity of germline SVs was recurrently and significantly associated with differential expression in the tumor sample across multiple patients.

Results: For hundreds of genes, recurrent and common germline SV breakpoints within 1 Mb were associated with higher or lower expression in tumors spanning various histologic types. Some germline SV-expression associations involved gene deletion or disruption, while others represented cis-regulatory alterations. Rare and singleton SVs disrupting DNA repair-related and mitochondrial-related genes collectively involved 2.7 and 4.7% of patients, respectively. Genes with germline SV breakpoint patterns and expression associated with patients of African ancestry included ACOT1 and CRYBB2P1. Genes with germline SV breakpoint patterns and expression associated with patient survival included ACTG1 and AHRR. Genes altered in association with both somatic and germline SVs included HGF and BCOR.

Conclusion: Our results capture a class of phenotypic variation at work in the setting of pediatric brain tumors, including genes with cancer roles.

Keywords

Humans, Brain Neoplasms, Child, Transcriptome, Male, Female, Germ-Line Mutation, Genomic Structural Variation, Child, Preschool, Adolescent

Published Open-Access

yes

Share

COinS
 
 

To view the content in your browser, please download Adobe Reader or, alternately,
you may Download the file to your hard drive.

NOTE: The latest versions of Adobe Reader do not support viewing PDF files within Firefox on Mac OS and if you are using a modern (Intel) Mac, there is no official plugin for viewing PDF files within the browser window.